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Next Generation

Gene Therapy

Genosera is revolutionizing gene therapy with next generation treatments that can stop progression, reverse, and even cure diseases while improving quality of life.

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ABOUT US

Advancing Today.
Transforming Tomorrow.

Genosera is a gene therapy biotechnology company founded in 2019. We are focused on developing cutting-edge treatments for rare diseases and difficult disease applications.

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Our mission is to develop safe, effective, and affordable therapies that have the potential to transform lives and create lasting impact for patients and families worldwide.

OUR FOCUS

Targeting Rare Diseases with High Unmet Need

GNE Myopathy (GNEM) Rare Muscle Disease

A rare, progressive myopathy caused by mutations in the GNE gene, leading to muscle weakness and wasting. Our gene therapy candidate aims to restore GNE function and improve muscle strength.​​​​

Explore Our Focus

Lysosomal Acid Lipase Deficiency (LAL-D)

A rare genetic disorder that affects the body's ability to break down cholesterol esters and triglycerides. Our therapy is designed to restore enzyme activity and prevent disease progression.

Explore Our Science

Limb-Girdle Muscular Dystrophy Type 2I (LGMD2I)

A debilitating muscle-wasting disease caused by FKRP gene mutations. Our gene therapy approach seeks to restore dystroglycan function and preserve muscle integrity and mobility.

Explore Our Pipeline
OUR SCIENCE

What is Gene Therapy?

Gene therapy is a medical approach that treats or prevents disease by replacing, inactivating, or modifying genes within a patient's cells. It has the potential to address the root cause of genetic disorders.

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Our Gene Therapy Platform

Genosera is developing next generation gene therapies using an AAV-based delivery platform with a patent-pending dual-gene design. Our platform enables efficient delivery of multiple genes.

LET'S CONNECT

Ready to Learn More?

We're here to answer your questions and explore how we can work together to advance the future of gene therapy.

Address

1275 Kinnear Road, Columbus, OH 43212

Office Hours

Mon - Fri: 8am - 5pm EST

Your Support Drives Discovery

Every contribution helps us bring life-changing therapies to patients who need them most. Join our mission today. Together, we can accelerate breakthroughs and create a healthier future for generations to come.

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